{"id":13400,"date":"2026-05-19T21:57:17","date_gmt":"2026-05-19T21:57:17","guid":{"rendered":"https:\/\/medical-article.com\/?p=13400"},"modified":"2026-05-19T21:57:17","modified_gmt":"2026-05-19T21:57:17","slug":"biomarins-mixed-bag-of-phase-3-data-dim-prospects-for-rare-disease-drug","status":"publish","type":"post","link":"https:\/\/medical-article.com\/?p=13400","title":{"rendered":"BioMarin\u2019s Mixed Bag of Phase 3 Data Dim Prospects for Rare Disease Drug"},"content":{"rendered":"<p><a href=\"https:\/\/medcitynews.com\/2026\/05\/biomarin-pharmaceutical-rare-disease-enpp1-enzyme-deficiency-rickets-bmrn\/\"><\/a><\/p>\n<p>A BioMarin Pharmaceutical drug met just one of two main goals of a Phase 3 test in a rare inherited enzyme deficiency with no FDA-approved therapies. The drug, a fusion protein, came from BioMarin\u2019s 2025 acquisition of Inozyme Pharma.<\/p>\n<p>The post <a href=\"https:\/\/medcitynews.com\/2026\/05\/biomarin-pharmaceutical-rare-disease-enpp1-enzyme-deficiency-rickets-bmrn\/\">BioMarin\u2019s Mixed Bag of Phase 3 Data Dim Prospects for Rare Disease Drug<\/a> appeared first on <a href=\"https:\/\/medcitynews.com\/\">MedCity News<\/a>.<\/p>","protected":false},"excerpt":{"rendered":"<p>A BioMarin Pharmaceutical drug met just one of two main goals of a Phase 3 test in a rare inherited enzyme deficiency with no FDA-approved therapies. The drug, a fusion protein, came from BioMarin\u2019s 2025 acquisition of Inozyme Pharma. The post BioMarin\u2019s Mixed Bag of Phase 3 Data Dim Prospects for Rare Disease Drug appeared&#8230;<\/p>\n","protected":false},"author":0,"featured_media":13401,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[4],"tags":[],"class_list":["post-13400","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-medicine"],"_links":{"self":[{"href":"https:\/\/medical-article.com\/index.php?rest_route=\/wp\/v2\/posts\/13400"}],"collection":[{"href":"https:\/\/medical-article.com\/index.php?rest_route=\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/medical-article.com\/index.php?rest_route=\/wp\/v2\/types\/post"}],"replies":[{"embeddable":true,"href":"https:\/\/medical-article.com\/index.php?rest_route=%2Fwp%2Fv2%2Fcomments&post=13400"}],"version-history":[{"count":0,"href":"https:\/\/medical-article.com\/index.php?rest_route=\/wp\/v2\/posts\/13400\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/medical-article.com\/index.php?rest_route=\/wp\/v2\/media\/13401"}],"wp:attachment":[{"href":"https:\/\/medical-article.com\/index.php?rest_route=%2Fwp%2Fv2%2Fmedia&parent=13400"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/medical-article.com\/index.php?rest_route=%2Fwp%2Fv2%2Fcategories&post=13400"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/medical-article.com\/index.php?rest_route=%2Fwp%2Fv2%2Ftags&post=13400"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}