{"id":8413,"date":"2025-09-23T16:46:13","date_gmt":"2025-09-23T16:46:13","guid":{"rendered":"https:\/\/medical-article.com\/?p=8413"},"modified":"2025-09-23T16:46:13","modified_gmt":"2025-09-23T16:46:13","slug":"ionis-pharmas-drug-for-rare-disease-with-no-approved-therapies-meets-goals-of-pivotal-study","status":"publish","type":"post","link":"https:\/\/medical-article.com\/?p=8413","title":{"rendered":"Ionis Pharma\u2019s Drug for Rare Disease With No Approved Therapies Meets Goals of Pivotal Study"},"content":{"rendered":"<p><a href=\"https:\/\/medcitynews.com\/2025\/09\/ionis-alexander-disease-zilganersen-antisense-oligonucleotide-aso-rare-disease-axd-ions\/\"><\/a><\/p>\n<p>Ionis Pharmaceuticals plans a 2026 FDA submission for zilganersen as a treatment for Alexander disease, an ultra-rare inherited neurological disorder. The antisense oligonucleotide developer has been moving toward commercializing drugs on its own rather than seeking partners. <\/p>\n<p>The post <a href=\"https:\/\/medcitynews.com\/2025\/09\/ionis-alexander-disease-zilganersen-antisense-oligonucleotide-aso-rare-disease-axd-ions\/\">Ionis Pharma\u2019s Drug for Rare Disease With No Approved Therapies Meets Goals of Pivotal Study<\/a> appeared first on <a href=\"https:\/\/medcitynews.com\/\">MedCity News<\/a>.<\/p>","protected":false},"excerpt":{"rendered":"<p>Ionis Pharmaceuticals plans a 2026 FDA submission for zilganersen as a treatment for Alexander disease, an ultra-rare inherited neurological disorder. The antisense oligonucleotide developer has been moving toward commercializing drugs on its own rather than seeking partners. The post Ionis Pharma\u2019s Drug for Rare Disease With No Approved Therapies Meets Goals of Pivotal Study appeared&#8230;<\/p>\n","protected":false},"author":0,"featured_media":8414,"comment_status":"open","ping_status":"open","sticky":false,"template":"","format":"standard","meta":{"footnotes":""},"categories":[4],"tags":[],"class_list":["post-8413","post","type-post","status-publish","format-standard","has-post-thumbnail","hentry","category-medicine"],"_links":{"self":[{"href":"https:\/\/medical-article.com\/index.php?rest_route=\/wp\/v2\/posts\/8413"}],"collection":[{"href":"https:\/\/medical-article.com\/index.php?rest_route=\/wp\/v2\/posts"}],"about":[{"href":"https:\/\/medical-article.com\/index.php?rest_route=\/wp\/v2\/types\/post"}],"replies":[{"embeddable":true,"href":"https:\/\/medical-article.com\/index.php?rest_route=%2Fwp%2Fv2%2Fcomments&post=8413"}],"version-history":[{"count":0,"href":"https:\/\/medical-article.com\/index.php?rest_route=\/wp\/v2\/posts\/8413\/revisions"}],"wp:featuredmedia":[{"embeddable":true,"href":"https:\/\/medical-article.com\/index.php?rest_route=\/wp\/v2\/media\/8414"}],"wp:attachment":[{"href":"https:\/\/medical-article.com\/index.php?rest_route=%2Fwp%2Fv2%2Fmedia&parent=8413"}],"wp:term":[{"taxonomy":"category","embeddable":true,"href":"https:\/\/medical-article.com\/index.php?rest_route=%2Fwp%2Fv2%2Fcategories&post=8413"},{"taxonomy":"post_tag","embeddable":true,"href":"https:\/\/medical-article.com\/index.php?rest_route=%2Fwp%2Fv2%2Ftags&post=8413"}],"curies":[{"name":"wp","href":"https:\/\/api.w.org\/{rel}","templated":true}]}}