Ultragenyx Gene Therapy Is First Approved Treatment for Rare Neuro Disease Sanfilippo
Ultragenyx Pharmaceutical’s Fayuvi is now the first FDA-approved therapy for the underlying cause of Sanfilippo…
Ultragenyx Gene Therapy Is First Approved Treatment for Rare Neuro Disease Sanfilippo
Ultragenyx Pharmaceutical’s Fayuvi is now the first FDA-approved therapy for the underlying cause of Sanfilippo syndrome type A, an ultra-rare inherited neurological disorder. It’s the second approved gene therapy for Ultragenyx, which specializes in rare disease medicines. The post Ultragenyx Gene Therapy Is First Approved Treatment for Rare Neuro Disease Sanfilippo appeared first on MedCity…
MultiCare Health System Takes Platform-Based Approach to Data Orchestration
Nick Shepard, health system’s assistant vice president of data orchestration, says rapid growth led to partnership with vendor ELLKAY to scale integration work
CMS Broadens ACCESS Model to New Chronic Conditions
CMS will expand its ACCESS model starting in spring 2027 to cover heart failure, COPD, substance use disorders and tobacco cessation. The outcomes-based payment model, which launched in July with 160 participating providers, will now make roughly three in four Medicare beneficiaries eligible for at least one track. The post CMS Broadens ACCESS Model to…
A Closer Look at the $50 Billion Rural Health Transformation Program
The 2025 budget reconciliation created the Rural Health Transformation Program, which will award $50 billion in state grants over a five-year period. This brief provides an overview of the program, describing its structure, how funds can be used, how funding compares to Medicaid spending reductions in the reconciliation law, and how the funds are being…
Extending ADHD Coverage for the Entire Active Day
The next evolution in ADHD therapy needs to focus not only on drug efficacy but also on how treatment aligns with the ever-busy and demanding lives of patients, families, and caregivers. The post Extending ADHD Coverage for the Entire Active Day appeared first on MedCity News.
State Fiscal Conditions: Context on Medicaid Budgets for FY 2027
This brief describes current fiscal conditions using the latest state revenue and spending data from the National Association of State Budget Officers (NASBO) and analyzes how these conditions may impact states’ Medicaid budget decisions going forward.
The Shifting Role of Wearables in Healthcare
The INVEST Digital Health conference, which will spotlight the consumer influence in healthcare, will include a discussion on wearables. It is scheduled for October 29 at Pegasus Park in Dallas. Register today! The post The Shifting Role of Wearables in Healthcare appeared first on MedCity News.
Sticker Shock at the Doctor’s Office Could Motivate Midterm Voters
Healthcare prices are likely to keep increasing next year. As midterm elections approach, candidates are laying out their plans to tackle these growing expenses. KFF Health News chief Washington correspondent Julie Rovner joined WAMU’s Health Hub on Sept. 16 to explain how healthcare could play a critical role in the midterm elections. She said similar…
The Drugs and Devices Have Been on the Market for Years. But FDA-Ordered Studies Still Aren’t Done.
When the FDA was deciding whether to approve the drug Tavneos several years ago to treat a set of rare autoimmune diseases, agency experts argued that would be a mistake, according to FDA records. One problem cited: The manufacturer had provided only “limited safety data.” As it often does, the FDA in 2021 approved the…
Cost-Saving Medicaid Meal Deliveries Threatened by Cuts, Policy Uncertainty
On a weekday morning in a quiet Boston neighborhood, a kitchen bustled with activity. Volunteers sliced chicken breasts, stuffed bell peppers, filled trays, and carefully labeled each item. It was part of an experiment to offer nutritious and medically tailored meals to Medicaid patients who are unable to shop for groceries and cook for themselves….
